Genetic / familial dilated cardiomyopathy (LMNA/FLNC/TTN/RBM20/DSP, chronic)
Encounter flow
12/12 authoredCanonical 12-phase frame with authored status for this dossier.
Frame
Establish genetic/familial DCM + genotype — genotype drives ICD threshold + prognosis
genetic DCM + genotype framed
Patient inputs (11)
Pediatric/young more severe; surveillance cadence
Cascade screening + inheritance pattern
LMNA/FLNC/DSP/RBM20/PLN/TMEM43 (arrhythmogenic, low ICD threshold) vs TTN (standard) — management-defining
GDMT + standard ICD criteria; arrhythmogenic genotypes override at higher EF
Functional status + GDMT/transplant timing
GDMT dosing
LGE burden refines arrhythmic/SCD risk (esp. DSP/FLNC)
Alcohol/tachycardia/peripartum/toxin — treat, but genetic substrate persists
AF common (esp. LMNA) — rate/rhythm + anticoagulation
AV conduction disease — LMNA risk-model component + ICD-capable device decision
Non-sustained VT — LMNA risk-model component + arrhythmic risk
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Severity triggers (9)
- informationallife_threateninglmna_low_icd_thresholdLMNA cardiomyopathy — conduction disease + malignant VT often before LV dysfunction; ICD by LMNA risk model even at EF >35; if pacing indicated use ICD-capable device — Wahbi JACC 2019Trigger could not be auto-evaluated — needs clinician judgement.
- informationallife_threateningend_stage_transplant_lvadEnd-stage genetic DCM (LMNA often progresses despite GDMT) — transplant / durable LVAD evaluation — 2023 ESC CardiomyopathyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalsevereflnc_dsp_rbm20_arrhythmicFLNC-truncating / DSP / RBM20 / PLN / TMEM43 — arrhythmic DCM, high LGE/SCD; low ICD threshold; DSP "hot phases" mimic myocarditis — 2023 ESC CardiomyopathyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalseveregdmt_withdrawal_relapseRecovered EF on GDMT in genetic DCM — do NOT withdraw therapy (TRED-HF relapse, genetic substrate persists) → route HF-improved engine — TRED-HF Lancet 2019Trigger could not be auto-evaluated — needs clinician judgement.
- informationalseverepregnancy_special_popPregnancy with genetic DCM — peripartum unmasking/decompensation; STOP ACEi/ARB/ARNi/SGLT2i → BB ± hydralazine; LMNA arrhythmic risk; cardio-obstetric — ESC 2018 PregnancyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalmoderatettn_gdmt_responsiveTTN-truncating DCM — GDMT-responsive with good reverse-remodeling; ICD by STANDARD EF criteria (not low-threshold) — 2023 ESC CardiomyopathyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalmoderategene_positive_phenotype_negativePathogenic-variant carrier without phenotype — serial surveillance (echo/ECG/Holter); exercise restriction if arrhythmogenic genotype — 2023 ESC CardiomyopathyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalmoderatereversible_contributor_branchCoexisting alcohol/tachycardia/toxin contributor in genetic DCM — treat the reversible factor but maintain genetic-substrate management (do not assume cure) — 2023 ESC CardiomyopathyTrigger could not be auto-evaluated — needs clinician judgement.
- informationalmoderateckd_special_popCKD — GDMT dose-gating — KDIGO 2024Trigger could not be auto-evaluated — needs clinician judgement.
Workflow calculators
Run this disease's risk and dosing calculators inline.
Recommended regimen
Genetic DCM — HFrEF GDMT + genotype-specific ICD (2022 AHA/ACC/HFSA; 2023 ESC Cardiomyopathy)- sacubitril/valsartanfirst lineARNi24/26→97/103 mg • PO • BIDtriggers: LVEF<=40, SBP>=100Standard HFrEF GDMT applies — TTN-truncating DCM is particularly GDMT-responsive (PARADIGM-HF; 2022 ACC/AHA HF)rxcui 1656340
- carvedilolfirst linebeta_blocker3.125→25 mg • PO • BIDtriggers: LVEF<=40Evidence-based BB pillar (2022 ACC/AHA HF)rxcui 20352
- spironolactonefirst lineMRA12.5–25 mg • PO • once dailytriggers: LVEF<=40, K<=5.0MRA pillar (2022 ACC/AHA HF)rxcui 9997
- dapagliflozinfirst lineSGLT2i10 mg • PO • once dailytriggers: eGFR>=20SGLT2i pillar (2022 ACC/AHA HF)rxcui 1488564
outpatient playbook — drug actions (3)
- 1. 4-pillar HFrEF GDMTper HFrEF protocol • PO • per drugtrigger: LVEF ≤40 (2022 ACC/AHA HF)Disease-modifying — esp. TTN reverse remodeling
- 2. genotype-specific ICDdevice • device • n/atrigger: Arrhythmogenic genotype with risk / EF ≤35 / sustained VA (2023 ESC Cardiomyopathy)Low threshold; ICD-capable if pacing needed in LMNA
- 3. amiodarone ± ablation for VAamiodarone load→200 mg/day • PO • dailytrigger: Recurrent VA (2023 ESC Cardiomyopathy)VA suppression; does not replace ICD
Auto-drafted A&P note
outpatientSubjective
- Possible entry pathways: Echo: dilated LV + systolic dysfunction (non-ischemic); Family history of DCM / unexplained SCD / known pathogenic variant; AV block / conduction disease with DCM (LMNA flag).
Objective
- No vitals, labs, or imaging entered for this encounter.
Assessment
**Genetic / familial dilated cardiomyopathy (LMNA/FLNC/TTN/RBM20/DSP, chronic)** (cardio.dcm-genetic.chronic.v1). Phenotype framing: Genetic DCM vs acquired DCM vs ARVC/ALVC vs LVNC vs myocarditis Scope: Establish genetic/familial DCM + genotype — genotype drives ICD threshold + prognosis No severity triggers fired against current inputs.
Plan
Regimen axis: **Genetic DCM — HFrEF GDMT + genotype-specific ICD (2022 AHA/ACC/HFSA; 2023 ESC Cardiomyopathy)** — step "Step 1 — HFrEF 4-pillar GDMT for systolic dysfunction (TTN best reverse-remodeling)". 1. sacubitril/valsartan 24/26→97/103 mg PO BID (ARNi, first line) — Standard HFrEF GDMT applies — TTN-truncating DCM is particularly GDMT-responsive (PARADIGM-HF; 2022 ACC/AHA HF) 2. carvedilol 3.125→25 mg PO BID (beta_blocker, first line) — Evidence-based BB pillar (2022 ACC/AHA HF) 3. spironolactone 12.5–25 mg PO once daily (MRA, first line) — MRA pillar (2022 ACC/AHA HF) 4. dapagliflozin 10 mg PO once daily (SGLT2i, first line) — SGLT2i pillar (2022 ACC/AHA HF) Setting playbook (outpatient) — GDMT for systolic dysfunction + genotype-specific ICD + cascade screening + exercise counseling (2022 AHA/ACC/HFSA; 2023 ESC Cardiomyopathy) 5. 4-pillar HFrEF GDMT per HFrEF protocol PO per drug — LVEF ≤40 (2022 ACC/AHA HF) (Disease-modifying — esp. TTN reverse remodeling) 6. genotype-specific ICD device device n/a — Arrhythmogenic genotype with risk / EF ≤35 / sustained VA (2023 ESC Cardiomyopathy) (Low threshold; ICD-capable if pacing needed in LMNA) 7. amiodarone ± ablation for VA amiodarone load→200 mg/day PO daily — Recurrent VA (2023 ESC Cardiomyopathy) (VA suppression; does not replace ICD) Non-pharmacologic actions: - Genetic counseling + first-degree family cascade screening + serial carrier evaluation — 2023 ESC Cardiomyopathy - Exercise restriction in arrhythmogenic genotypes (LMNA/FLNC/DSP) — 2023 ESC Cardiomyopathy - Inherited-cardiomyopathy centre + EP referral — 2023 ESC Cardiomyopathy - Do NOT withdraw GDMT on EF recovery (TRED-HF) — Halliday Lancet 2019 AVOID / contraindication checks: - Low ICD threshold in LMNA FLNC DSP RBM20 even at EF gt 35 — 2022 AHA/ACC/HFSA; 2023 ESC Cardiomyopathy - Use ICD capable device if pacing indicated in LMNA — 2023 ESC Cardiomyopathy - Do not withdraw GDMT on recovery in genetic DCM — TRED HF Halliday Lancet 2019 - Exercise restriction in arrhythmogenic DCM genotypes — 2023 ESC Cardiomyopathy - Treat reversible contributors but genetic substrate persists — 2023 ESC Cardiomyopathy
Monitoring
Regimen monitoring: - serial echo LVEF and Holter genotype specific cadence — 2023 ESC Cardiomyopathy - LMNA risk model reassessment for ICD — Wahbi JACC 2019 - do not withdraw GDMT on recovery — TRED-HF Lancet 2019 - first degree family cascade and serial carrier evaluation — 2023 ESC Cardiomyopathy - BMP during GDMT titration — 2022 ACC/AHA HF Setting (outpatient) monitoring: - Serial echo/Holter genotype-specific; LMNA risk reassessment — Wahbi JACC 2019 - BMP during GDMT titration — 2022 ACC/AHA HF Follow-up plan: First-degree family cascade screening + serial evaluation of gene-positive relatives; lifelong genotype-specific care - Close-out criterion: cascade + long-term plan documented Monitoring phase: Serial echo/Holter; genotype-specific cadence; do-not-withdraw GDMT on recovery (TRED-HF)
Disposition
Current setting: outpatient — GDMT for systolic dysfunction + genotype-specific ICD + cascade screening + exercise counseling (2022 AHA/ACC/HFSA; 2023 ESC Cardiomyopathy) Disposition criteria: - Genetic DCM → GDMT + genotype-specific ICD decision + cascade - Gene-positive phenotype-negative → surveillance + exercise counseling - End-stage → transplant/LVAD evaluation Escalation triggers (move to higher acuity): - High-grade AV block in LMNA → ICD-capable device (not PPM-only) — 2023 ESC Cardiomyopathy - Sustained VT/VF → EP + ICD — 2023 ESC Cardiomyopathy - Progressive end-stage (esp. LMNA) → transplant/LVAD — 2023 ESC Cardiomyopathy
Earlier-Return Triggers
Return-precaution thresholds (watch for): - [LIFE_THREATENING] LMNA cardiomyopathy — conduction disease + malignant VT often before LV dysfunction; ICD by LMNA risk model even at EF >35; if pacing indicated use ICD-capable device — Wahbi JACC 2019 - [LIFE_THREATENING] End-stage genetic DCM (LMNA often progresses despite GDMT) — transplant / durable LVAD evaluation — 2023 ESC Cardiomyopathy - [SEVERE] FLNC-truncating / DSP / RBM20 / PLN / TMEM43 — arrhythmic DCM, high LGE/SCD; low ICD threshold; DSP "hot phases" mimic myocarditis — 2023 ESC Cardiomyopathy
Citations
- 2023 ESC Cardiomyopathy Guideline + 2022 AHA/ACC/HFSA HF Guideline; Wahbi LMNA risk model; TRED-HF [PMID:37622657](https://pubmed.ncbi.nlm.nih.gov/37622657/) - Cited evidence (PMID 35379504) [PMID:35379504](https://pubmed.ncbi.nlm.nih.gov/35379504/) - Cited evidence (PMID 30871198) [PMID:30871198](https://pubmed.ncbi.nlm.nih.gov/30871198/) - Cited evidence (PMID 30429050) [PMID:30429050](https://pubmed.ncbi.nlm.nih.gov/30429050/) - Cited evidence (PMID 31535829) [PMID:31535829](https://pubmed.ncbi.nlm.nih.gov/31535829/) Last reconciled with current guidelines: 2026-05-16.
- 2023 ESC Cardiomyopathy Guideline + 2022 AHA/ACC/HFSA HF Guideline; Wahbi LMNA risk model; TRED-HF — PMID:37622657
- Cited evidence (PMID 35379504) — PMID:35379504
- Cited evidence (PMID 30871198) — PMID:30871198
- Cited evidence (PMID 30429050) — PMID:30429050
- Cited evidence (PMID 31535829) — PMID:31535829